CHU Dijon, Service de Cardiologie, Hôpital le Bocage, Dijon, France.
J Am Coll Cardiol. 2012 Jul 10;60(2):144-56. doi: 10.1016/j.jacc.2012.02.052.
The aim of this study was to describe a new familial cardiac phenotype and to elucidate the electrophysiological mechanism responsible for the disease.
Mutations in several genes encoding ion channels, especially SCN5A, have emerged as the basis for a variety of inherited cardiac arrhythmias.
Three unrelated families comprising 21 individuals affected by multifocal ectopic Purkinje-related premature contractions (MEPPC) characterized by narrow junctional and rare sinus beats competing with numerous premature ventricular contractions with right and/or left bundle branch block patterns were identified.
Dilated cardiomyopathy was identified in 6 patients, atrial arrhythmias were detected in 9 patients, and sudden death was reported in 5 individuals. Invasive electrophysiological studies demonstrated that premature ventricular complexes originated from the Purkinje tissue. Hydroquinidine treatment dramatically decreased the number of premature ventricular complexes. It normalized the contractile function in 2 patients. All the affected subjects carried the c.665G>A transition in the SCN5A gene. Patch-clamp studies of resulting p.Arg222Gln (R222Q) Nav1.5 revealed a net gain of function of the sodium channel, leading, in silico, to incomplete repolarization in Purkinje cells responsible for premature ventricular action potentials. In vitro and in silico studies recapitulated the normalization of the ventricular action potentials in the presence of quinidine.
A new SCN5A-related cardiac syndrome, MEPPC, was identified. The SCN5A mutation leads to a gain of function of the sodium channel responsible for hyperexcitability of the fascicular-Purkinje system. The MEPPC syndrome is responsive to hydroquinidine.
本研究旨在描述一种新的家族性心脏表型,并阐明导致该疾病的电生理机制。
编码离子通道的几个基因(尤其是 SCN5A)的突变已成为多种遗传性心律失常的基础。
鉴定了三个不相关的家族,共 21 名个体受多灶性异位浦肯野相关过早收缩(MEPPC)影响,其特征为窄结和罕见的窦性搏动与大量具有右和/或左束支传导阻滞模式的室性早搏竞争。
6 名患者诊断为扩张型心肌病,9 名患者检测到心房心律失常,5 名患者报告猝死。侵入性电生理研究表明,室性早搏起源于浦肯野组织。氢氯喹治疗显著减少了室性早搏的数量。它使 2 名患者的收缩功能正常化。所有受影响的个体均携带 SCN5A 基因的 c.665G>A 转换。对由此产生的 p.Arg222Gln(R222Q)Nav1.5 的膜片钳研究显示钠通道的功能获得,导致浦肯野细胞中的不完全复极,从而导致室性动作电位过早。在体外和计算机模拟中,奎尼丁的存在使心室动作电位正常化。
鉴定了一种新的 SCN5A 相关心脏综合征,即 MEPPC。SCN5A 突变导致钠通道功能获得,导致束支-浦肯野系统的过度兴奋。MEPPC 综合征对氢氯喹有反应。