AP-HP Centre, Hôpital Cochin, Service de Pneumologie, Paris, France.
Université de Paris, Institut Cochin, INSERM UMR 1016, Paris, France.
Int J Chron Obstruct Pulmon Dis. 2021 Aug 16;16:2363-2373. doi: 10.2147/COPD.S226688. eCollection 2021.
Current pharmacological treatments for chronic obstructive pulmonary disease (COPD) are mostly limited to inhaled bronchodilators and corticosteroids. Azithromycin can contribute to exacerbation prevention. Roflumilast, a phosphodiesterase (PDE) 4 inhibitor administered orally, also prevents exacerbations in selected patients with chronic bronchitis, recurrent exacerbations, severe airflow limitation and concomitant therapy with long-acting inhaled bronchodilators. This outcome likely results from anti-inflammatory effects since PDE4 is expressed by all inflammatory cell types involved in COPD. The use of this agent is, however, limited by side-effects, particularly nausea and diarrhea. To address remaining unmet needs and enrich therapeutic options for patients with COPD, inhaled dual PDE3/4 inhibitors have been developed, with the aim of enhancing bronchodilation through PDE3 inhibition and modulating inflammation and mucus production though PDE4 inhibition, thus producing a potentially synergistic effect on airway calibre. Experimental preclinical data confirmed these effects in vitro and in animal models. At present, RPL554/ensifentrine is the only agent of this family in clinical development. It decreases sputum markers of both neutrophilic and eosinophilic inflammation in patients with COPD. Clinical Phase II trials confirmed its bronchodilator effect and demonstrated clinically meaningful symptom relief and quality of life improvements in these patients. The safety profile appears satisfactory, with less effects on heart rate and blood pressure than salbutamol and no other side effect. Altogether, these data suggest that ensifentrine could have a role in COPD management, especially in addition to inhaled long-acting bronchodilators with or without corticosteroids since experimental studies suggest potentiation of ensifentrine effects by these agents. However, results from ongoing and future Phase III studies are needed to confirm both beneficial effects and favourable safety profile on a larger scale and assess other outcomes including exacerbations, lung function decline, comorbidities and mortality.
目前,慢性阻塞性肺疾病(COPD)的药物治疗大多局限于吸入性支气管扩张剂和皮质类固醇。阿奇霉素可有助于预防加重。罗氟司特,一种磷酸二酯酶(PDE)4 抑制剂,口服给药,也可预防慢性支气管炎、反复加重、严重气流受限和长效吸入性支气管扩张剂联合治疗的患者的加重。这种结果可能是由于抗炎作用所致,因为 PDE4 表达于 COPD 所有参与炎症的细胞类型。然而,该药物的使用受到副作用的限制,特别是恶心和腹泻。为了解决 COPD 患者未满足的需求并丰富治疗选择,已开发出吸入性双重 PDE3/4 抑制剂,旨在通过 PDE3 抑制增强支气管扩张,并通过 PDE4 抑制调节炎症和粘液产生,从而对气道口径产生潜在的协同作用。实验性临床前数据在体外和动物模型中证实了这些作用。目前,RPL554/ensifentrine 是该家族中唯一处于临床开发阶段的药物。它可降低 COPD 患者痰液中中性粒细胞和嗜酸性粒细胞炎症的标志物。临床 II 期试验证实了其支气管扩张作用,并在这些患者中显示出有临床意义的症状缓解和生活质量改善。安全性特征似乎令人满意,与沙丁胺醇相比,对心率和血压的影响较小,且无其他副作用。总的来说,这些数据表明 ensifentrine 可能在 COPD 管理中发挥作用,尤其是在吸入长效支气管扩张剂联合或不联合皮质类固醇的基础上,因为实验研究表明这些药物可增强 ensifentrine 的作用。然而,需要正在进行和未来的 III 期研究的结果来在更大范围内证实其有益效果和良好的安全性特征,并评估其他结局,包括加重、肺功能下降、合并症和死亡率。