Department of Pathology, Faculty of Medicine in Pilsen, Charles University, E. Benese 13, 305 99, Pilsen, Czech Republic.
Bioptic Laboratory, Ltd., Pilsen, Czech Republic.
Virchows Arch. 2024 Aug;485(2):245-256. doi: 10.1007/s00428-023-03650-2. Epub 2023 Dec 12.
SMARCB1-deficient sinonasal adenocarcinoma is a rare variant of SWI/SNF-deficient malignancies with SMARCB1 loss and adenocarcinoma features. More than 200 high-grade epithelial sinonasal malignancies were retrieved. A total of 14 cases exhibited complete SMARCB1 (INI1) loss and glandular differentiation. SMARCA2 and SMARCA4 were normal, except for one case with a loss of SMARCA2. Next-generation sequencing (NGS) and/or fluorescence in situ hybridization (FISH) revealed an alteration in the SMARCB1 gene in 9/13 cases, while 2/13 were negative. Two tumors harbored SMARCB1 mutations in c.157C > T p.(Arg53Ter) and c.842G > A p.(Trp281Ter). One harbored ARID1B mutations in c.1469G > A p.(Trp490Ter) and MGA c.3724C > T p.(Arg1242Ter). Seven tumors had a SMARCB1 deletion. One carried an ESR1 mutation in c.644-2A > T, and another carried a POLE mutation in c.352_374del p.(Ser118GlyfsTer78). One case had a PAX3 mutation in c.44del p.(Gly15AlafsTer95). Histomorphology of SMARCB1-deficient adenocarcinoma was oncocytoid/rhabdoid and glandular, solid, or trabecular in 9/14 cases. Two had basaloid/blue cytoplasm and one showed focal signet ring cells. Yolk sac tumor-like differentiation with Schiller-Duval-like bodies was seen in 6/14 cases, with 2 cases showing exclusively reticular-microcystic yolk sac pattern. Follow-up of a maximum of 26 months (median 10 months) was available for 8/14 patients. Distant metastasis to the lung, liver, mediastinum, bone, and/or retroperitoneum was seen in 4/8 cases. Locoregional failure was seen in 75% of patients, with 6/8 local recurrences and 3 cervical lymph node metastases. At the last follow-up, 5 of 8 (62%) patients had died of their disease 2 to 20 months after diagnosis (median 8.2 months), and 3 were alive with the disease. The original diagnosis was usually high-grade non-intestinal-type adenocarcinoma or high-grade myoepithelial carcinoma. A correct diagnosis of these aggressive tumors could lead to improved targeted therapies with potentially better overall disease-specific survival.
SMARCB1 缺陷型鼻腔鼻窦腺癌是一种罕见的 SWI/SNF 缺陷性恶性肿瘤,具有 SMARCB1 缺失和腺癌特征。我们共检索到 200 多例高级别上皮性鼻腔鼻窦恶性肿瘤。共有 14 例完全缺失 SMARCB1(INI1)和腺分化。SMARCA2 和 SMARCA4 正常,除了 1 例 SMARCA2 缺失。下一代测序(NGS)和/或荧光原位杂交(FISH)显示,在 9/13 例中存在 SMARCB1 基因改变,而 2/13 例为阴性。2 个肿瘤在 c.157C>T p.(Arg53Ter)和 c.842G>A p.(Trp281Ter)处存在 SMARCB1 突变。1 个肿瘤存在 ARID1B 在 c.1469G>A p.(Trp490Ter)和 MGA c.3724C>T p.(Arg1242Ter)处的突变。7 个肿瘤存在 SMARCB1 缺失。1 个肿瘤存在 ESR1 在 c.644-2A>T 处的突变,另 1 个肿瘤存在 POLE 在 c.352_374del p.(Ser118GlyfsTer78)处的突变。1 个肿瘤存在 PAX3 在 c.44del p.(Gly15AlafsTer95)处的突变。SMARCB1 缺陷型腺癌的组织形态学为 9/14 例为类癌样/横纹肌样和腺性,实性或小梁状。2 例为基底细胞样/蓝色细胞质,1 例为局灶性印戒细胞样。6/14 例存在卵黄囊瘤样分化伴 Schiller-Duval 样小体,其中 2 例仅存在网状微囊状卵黄囊样模式。8/14 例患者中,有 26 个月(中位 10 个月)的最大随访时间。4/8 例患者出现肺、肝、纵隔、骨和/或腹膜后远处转移。75%的患者出现局部区域复发,其中 6/8 例局部复发,3 例出现颈部淋巴结转移。在最后一次随访时,8 例中有 5 例(62%)患者在诊断后 2 至 20 个月(中位 8.2 个月)死于疾病,3 例仍患有疾病。这些侵袭性肿瘤的正确诊断可能会导致更好的靶向治疗,从而提高总体疾病特异性生存率。