Guo Shujin, He Qiumei, Liu Yuping, Zou Aili, Liao Yang, Guo Li, Bai Lan, Shi Jianyou
Department of Health Management Center, Sichuan Academy of Medical Science & Sichuan Provincial People's Hospital, School of Medicine, University of Electronic Science and Technology of China, Chengdu, China.
The State Key Laboratory of Southwestern Chinese Medicine Resources, Department of Pharmacy, Chengdu University of Traditional Chinese Medicine, Chengdu, China.
Eur J Med Chem. 2025 Oct 15;296:117804. doi: 10.1016/j.ejmech.2025.117804. Epub 2025 May 24.
The DNA damage response (DDR) represents a promising target for cancer therapy, with key kinases like Ataxia telangiectasia and Rad3-related (ATR) playing a pivotal role in initiating DDR signaling. ATR activation triggers cell cycle arrest at the S and G2/M phases in response to DNA damage and replication stress (RS), facilitating cancer cell proliferation and inhibiting apoptosis. Numerous studies have identified ATR as a valuable target for anti-cancer strategies. Small molecule inhibitors targeting ATR have been synthesized and are currently undergoing clinical trials, both as monotherapies and in combination therapies. These inhibitors leverage synthetic lethality(SL) to selectively target cancer cells, enhancing anticancer efficacy and delaying drug resistance. This article offers a concise summary of ATR's structure and its role in DDR mechanisms. It also provides a detailed review of the structural characteristics, pharmacological profiles, and therapeutic or prophylactic potential of ATR small molecule inhibitors currently in clinical trials, including those with published chemical structures and inhibitors reported in patents from 2022 to 2024, offering valuable insights for the future development of safer and more effective ATR inhibitors.
DNA损伤反应(DDR)是癌症治疗的一个有前景的靶点,像共济失调毛细血管扩张症和Rad3相关蛋白(ATR)这样的关键激酶在启动DDR信号传导中起关键作用。ATR激活会触发细胞周期在S期和G2/M期停滞,以应对DNA损伤和复制应激(RS),促进癌细胞增殖并抑制细胞凋亡。众多研究已将ATR确定为抗癌策略的一个有价值的靶点。靶向ATR的小分子抑制剂已被合成,目前正在进行临床试验,包括单药治疗和联合治疗。这些抑制剂利用合成致死性(SL)来选择性地靶向癌细胞,提高抗癌疗效并延缓耐药性。本文简要概述了ATR的结构及其在DDR机制中的作用。它还详细综述了目前正在进行临床试验的ATR小分子抑制剂的结构特征、药理学概况以及治疗或预防潜力,包括那些具有已公布化学结构的抑制剂以及2022年至2024年专利中报道的抑制剂,为未来开发更安全、更有效的ATR抑制剂提供了有价值的见解。