Gehrig A, Felbor U, Kelsell R E, Hunt D M, Maumenee I H, Weber B H
Institut für Humangenetik, Biozentrum, Universität Würzburg, Germany.
J Med Genet. 1998 Aug;35(8):641-5. doi: 10.1136/jmg.35.8.641.
We have recently characterised the genomic organisation of a novel interphotoreceptor matrix proteoglycan, IMPG1, and have mapped the gene locus to chromosome 6q13-q15 by fluorescence in situ hybridisation. As the interphotoreceptor matrix (IPM) is thought to play a critical role in retinal adhesion and the maintenance of photoreceptor cells, it is conceivable that a defect in one of the IPM components may cause degenerative lesions in retinal structures and thus may be associated with human retinopathies. By genetic linkage analysis, several retinal dystrophies including one form of autosomal dominant Stargardt-like macular dystrophy (STGD3), progressive bifocal chorioretinal atrophy (PBCRA), and North Carolina macular dystrophy (MCDR1) have previously been localised to a region on proximal 6q that overlaps the IMPG1 locus. We have therefore assessed the entire coding region of IMPG1 by exon amplification and subsequent single stranded conformational analysis in patients from 6q linked multigeneration families diagnosed with PBCRA and MCDR1, as well as a single patient from an autosomal dominant STGD pedigree unlinked to either of the two known STGD2 and STGD3 loci on chromosomes 13q and 6q, respectively. No disease associated mutations were identified. In addition, using an intragenic polymorphism, IMPG1 was excluded by genetic recombination from both the PBCRA and the MCDR1 loci. However, as the autosomal dominant Stargardt-like macular dystrophies are genetically heterogeneous, other forms of this disorder, in particular STGD3 previously linked to 6q, may be caused by mutations in IMPG1.
我们最近对一种新型的光感受器间基质蛋白聚糖IMPG1的基因组结构进行了表征,并通过荧光原位杂交将该基因座定位到6号染色体的6q13 - q15区域。由于光感受器间基质(IPM)被认为在视网膜黏附和光感受器细胞的维持中起关键作用,因此可以想象IPM成分之一的缺陷可能导致视网膜结构的退行性病变,进而可能与人类视网膜病变相关。通过遗传连锁分析,包括一种常染色体显性遗传性Stargardt样黄斑营养不良(STGD3)、进行性双焦点脉络膜视网膜萎缩(PBCRA)和北卡罗来纳黄斑营养不良(MCDR1)在内的几种视网膜营养不良先前已被定位到6号染色体近端与IMPG1基因座重叠的区域。因此,我们通过外显子扩增和随后的单链构象分析,对来自诊断为PBCRA和MCDR1的6号染色体连锁多代家系的患者,以及来自一个常染色体显性遗传性STGD家系(该家系与分别位于13号染色体和6号染色体上的两个已知STGD2和STGD3基因座均无连锁关系)的一名患者,评估了IMPG1的整个编码区。未发现与疾病相关的突变。此外,利用基因内多态性,通过基因重组将IMPG1从PBCRA和MCDR1基因座中排除。然而,由于常染色体显性遗传性Stargardt样黄斑营养不良在遗传上具有异质性,这种疾病的其他形式,特别是先前与6号染色体连锁的STGD3,可能由IMPG1中的突变引起。