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With newer tools for gene editing, is it time to revisit genetic therapy for cystic fibrosis?

作者信息

Gupta Anuj, Gupta Ankita, Boyd Larissa

机构信息

Barts and the London School of Medicine and Dentistry, Institution address - Garrod Building, Turner Street, Whitechapel, E12AD, United Kingdom.

University of Birmingham, Birmingham Medical school, Edgbaston, B152TT, United Kingdom.

出版信息

Genes Dis. 2020 Jan 22;8(2):168-170. doi: 10.1016/j.gendis.2020.01.002. eCollection 2021 Mar.

Abstract
摘要

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本文引用的文献

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Repair of double-strand breaks induced by CRISPR-Cas9 leads to large deletions and complex rearrangements.
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