Department of Developmental Biology, Pennington Biomedical Research Center/Louisiana State University System, 6400 Perkins Road, Baton Rouge, LA, 70808, USA.
Department of Regulation of Gene Expression, Pennington Biomedical Research Center/Louisiana State University System, 6400 Perkins Road, Baton Rouge, LA, 70808, USA.
Sci Rep. 2021 Dec 9;11(1):23732. doi: 10.1038/s41598-021-02627-y.
Mendelian genetics poses practical limitations on the number of mutant genes that can be investigated simultaneously for their roles in embryonic development in the mouse. While CRISPR-based gene editing of multiple genes at once offers an attractive alternative strategy, subsequent breeding or establishment of permanent mouse lines will rapidly segregate the different mutant loci again. Direct phenotypic analysis of genomic edits in an embryonic lethal gene in F0 generation mice, or F0 mouse embryos, circumvents the need for breeding or establishment of mutant mouse lines. In the course of genotyping a large cohort of F0 CRISPants, where the embryonic lethal gene T/brachyury was targeted, we noted the presence of multiple CRISPR-induced modifications in individual embryos. Using long-read single-molecule Nanopore sequencing, we identified a wide variety of deletions, ranging up to 3 kb, that would not have been detected or scored as wildtype with commonly used genotyping methods that rely on subcloning and short-read or Sanger sequencing. Long-read sequencing results were crucial for accurate genotype-phenotype correlation in our F0 CRISPants. We thus demonstrate feasibility of screening manipulated F0 embryos for mid-gestation phenotypic consequences of CRISPR-induced mutations without requiring derivation of permanent mouse lines.
孟德尔遗传学对同时研究其在胚胎发育中的作用的突变基因数量存在实际限制。虽然基于 CRISPR 的多个基因的同时基因编辑提供了一种有吸引力的替代策略,但随后的繁殖或永久小鼠系的建立将再次迅速分离不同的突变基因座。在 F0 代小鼠或 F0 鼠胚胎中对胚胎致死基因的基因组编辑进行直接表型分析,避免了繁殖或建立突变小鼠系的需要。在对靶向胚胎致死基因 T/brachyury 的大量 F0 CRISPants 进行基因分型的过程中,我们注意到单个胚胎中存在多种 CRISPR 诱导的修饰。使用长读长单分子纳米孔测序,我们鉴定了多种缺失,范围高达 3kb,如果不依赖于亚克隆和短读长或 Sanger 测序的常用基因分型方法,这些缺失将不会被检测或判定为野生型。长读长测序结果对于我们的 F0 CRISPants 中准确的基因型-表型相关性至关重要。因此,我们证明了在不要求建立永久小鼠系的情况下,筛选经 CRISPR 诱导突变处理的 F0 胚胎以检测中期妊娠表型后果的可行性。