Department of Woman and Child's Health, University of Padova, Padova, Veneto, Italy.
Department of Pediatrics, Yale University, New Haven, Connecticut.
Pediatrics. 2022 Jul 1;150(1). doi: 10.1542/peds.2021-055671.
Insulin-resistant diabetes in Rabson-Mendenhall syndrome (RMS) is relatively unresponsive to first-line antidiabetic treatments, including metformin and insulin. We report 2 patients with RMS treated with 2 different sodium-glucose cotransporter inhibitors 2: empagliflozin in an 11-year-old boy and dapagliflozin in a 12-year-old girl. In the first patient, we began empagliflozin at 2.5 mg/day and increased the dose to 10 mg/day over 3 months. During treatment with empagliflozin, the amount of time during which the patient maintained serum glucose in the 70 to 180 mg/dL target range increased by 2 hours per day. Hemoglobin A1C dropped from >14% to 11.9%, urinary calcium increased almost twofold, and β-hydroxybutyrate remained <2.5 mmol/L. Because glycemic control did not further improve with dose escalation, we reverted to the 2.5 mg/day dose. We initiated dapagliflozin in a second patient at 5 mg/day and witnessed a reduction of hemoglobin A1C from 8.5% to 6.2% after 6 months and a mild increase in urinary excretion of phosphorus but not calcium. Insulin levels fell by >50%. In 2 patients with RMS, empagliflozin and dapagliflozin were well tolerated and improved glycemic control without significantly increasing ketonemia. Renal calcium excretion should be carefully monitored.
拉布森-门登霍尔综合征(RMS)中的胰岛素抵抗性糖尿病对一线抗糖尿病治疗(包括二甲双胍和胰岛素)反应相对较差。我们报告了 2 例 RMS 患者接受了 2 种不同的钠-葡萄糖共转运蛋白抑制剂治疗:11 岁男孩接受恩格列净治疗,12 岁女孩接受达格列净治疗。在第一个患者中,我们开始给予恩格列净 2.5 mg/天,并在 3 个月内将剂量增加至 10 mg/天。在恩格列净治疗期间,患者将血清葡萄糖维持在 70 至 180 mg/dL 目标范围内的时间增加了 2 小时/天。糖化血红蛋白从>14%降至 11.9%,尿钙增加近两倍,β-羟丁酸仍<2.5 mmol/L。由于剂量增加未能进一步改善血糖控制,我们恢复至 2.5 mg/天的剂量。我们在第二个患者中开始给予达格列净 5 mg/天,在 6 个月后观察到糖化血红蛋白从 8.5%降至 6.2%,尿磷排泄轻度增加,但钙排泄没有增加。胰岛素水平下降了>50%。在 2 例 RMS 患者中,恩格列净和达格列净均耐受良好,改善了血糖控制,而酮血症没有明显加重。应密切监测肾脏钙排泄。