enOsCas12f1-mediated exon skipping for Duchenne muscular dystrophy therapy in humanized mouse model.
作者信息
Jin Ming, Lin Jiajia, Zhang Yu, Xiao Qingquan, Kong Xiangfeng, Zhang Xiumei, Shao Zhurui, Wang Yin, Yu Yuyang, Li Jinjing, Chen Wan-Jin, Li Guoling, Yang Hui, Wang Ning
机构信息
Department of Neurology and Institute of Neurology of First Affiliated Hospital, Institute of Neuroscience, Fujian Key Laboratory of Molecular Neurology, Fujian Medical University, Fuzhou, Fujian 350004, China.
HUIDAGENE Therapeutics Co., Ltd., Shanghai 200131, China.
出版信息
J Genet Genomics. 2024 Feb;51(2):256-259. doi: 10.1016/j.jgg.2023.12.003. Epub 2023 Dec 14.
PMID:38103683
Abstract
摘要
Zotero 插件