Department of Cellular and Molecular Medicine, Centre for Neuromuscular Disease, Faculty of Medicine, University of Ottawa, Ottawa, Ontario, Canada.
FASEB J. 2018 Sep;32(9):5090-5103. doi: 10.1096/fj.201800081R. Epub 2018 May 3.
Duchenne muscular dystrophy (DMD) is a genetic and progressive neuromuscular disorder caused by mutations and deletions in the dystrophin gene. Although there is currently no cure, one promising treatment for DMD is aimed at increasing endogenous levels of utrophin A to compensate functionally for the lack of dystrophin. Recent studies from our laboratory revealed that heparin treatment of mdx mice activates p38 MAPK, leading to an upregulation of utrophin A expression and improvements in the dystrophic phenotype. Based on these findings, we sought to determine the effects of other potent p38 activators, including the cyclooxygenase (COX)-2 inhibitor celecoxib. In this study, we treated 6-wk-old mdx mice for 4 wk with celecoxib. Immunofluorescence analysis of celecoxib-treated mdx muscles revealed a fiber type switch from a fast to a slower phenotype along with beneficial effects on muscle fiber integrity. In agreement, celecoxib-treated mdx mice showed improved muscle strength. Celecoxib treatment also induced increases in utrophin A expression ranging from ∼1.5- to 2-fold in tibialis anterior diaphragm and heart muscles. Overall, these results highlight that activation of p38 in muscles can indeed lead to an attenuation of the dystrophic phenotype and reveal the potential role of celecoxib as a novel therapeutic agent for the treatment of DMD.-Péladeau, C., Adam, N. J., Jasmin, B. J. Celecoxib treatment improves muscle function in mdx mice and increases utrophin A expression.
杜氏肌营养不良症(DMD)是一种由抗肌萎缩蛋白基因突变和缺失引起的遗传性、进行性神经肌肉疾病。尽管目前尚无治愈方法,但一种有前途的 DMD 治疗方法旨在提高内源性 utrophin A 水平,以功能性补偿抗肌萎缩蛋白的缺乏。我们实验室最近的研究表明,肝素治疗 mdx 小鼠会激活 p38 MAPK,导致 utrophin A 表达上调,并改善肌营养不良表型。基于这些发现,我们试图确定其他强效 p38 激活剂的影响,包括环氧化酶(COX)-2 抑制剂塞来昔布。在这项研究中,我们用塞来昔布治疗 6 周龄的 mdx 小鼠 4 周。用塞来昔布处理的 mdx 肌肉的免疫荧光分析显示纤维类型从快肌向慢肌转变,同时对肌肉纤维完整性有有益影响。一致地,塞来昔布治疗的 mdx 小鼠显示出肌肉力量的改善。塞来昔布治疗还诱导 utrophin A 表达增加,在前胫骨肌和膈肌以及心肌中增加约 1.5 到 2 倍。总体而言,这些结果强调了肌肉中 p38 的激活确实可以导致肌营养不良表型的衰减,并揭示了塞来昔布作为治疗 DMD 的新型治疗剂的潜在作用。-Péladeau,C.,Adam,N. J.,Jasmin,B. J. 塞来昔布治疗可改善 mdx 小鼠的肌肉功能并增加 utrophin A 表达。