Department of Medicine III, Technische Universität Dresden Medical Center, Dresden, Germany.
Center for Healthy Aging, Technische Universität Dresden Medical Center, Dresden, Germany.
J Mol Endocrinol. 2019 Feb 1;62(2):R145-R154. doi: 10.1530/JME-18-0173.
Bone-forming approaches to treat patients with severe osteoporosis are effective, but treatment options are limited, and there is an unmet clinical need for additional drugs. This review discusses two novel and advanced anabolic therapeutic concepts that have successfully completed phase 3 trials. Romosozumab is a monoclonal antibody that targets the Wnt inhibitor sclerostin. Two phase 3 trials (FRAME and ARCH) of romosozumab for the treatment of postmenopausal osteoporosis have been completed. Both trials successfully reached their primary endpoint by reducing vertebral fractures by 75% compared to placebo (FRAME trial) and 48% compared to alendronate (ARCH trial), respectively. Abaloparatide is a PTH-related protein (PTHrP) analog that has displayed bone anabolic activity. In the phase 3 ACTIVE trial, abaloparatide was compared to placebo and teriparatide for 18 months in postmenopausal women who had already experienced an osteoporotic fracture. Abaloparatide successfully reduced the rate of new vertebral fractures by 86% compared to placebo. Furthermore, abaloparatide achieved greater BMD increases at all measured sites compared to both placebo and teriparatide. Based on these results, abaloparatide was FDA approved in April 2017. This review discusses available data of both agents with regard to efficacy and safety as well as their possible future application.
治疗严重骨质疏松症的成骨方法是有效的,但治疗选择有限,因此需要额外的药物来满足临床需求。这篇综述讨论了两种新型的先进的合成代谢治疗概念,它们已经成功完成了 3 期临床试验。罗莫佐单抗是一种针对 Wnt 抑制剂硬骨素的单克隆抗体。两项针对绝经后骨质疏松症的罗莫佐单抗 3 期临床试验(FRAME 和 ARCH)已经完成。这两项试验均成功达到了主要终点,与安慰剂相比,分别使椎体骨折减少了 75%(FRAME 试验)和 48%(ARCH 试验)。阿巴洛肽是一种甲状旁腺激素相关蛋白(PTHrP)类似物,具有骨合成代谢活性。在 3 期 ACTIVE 试验中,阿巴洛肽与安慰剂和特立帕肽在已经经历过骨质疏松性骨折的绝经后妇女中进行了 18 个月的比较。与安慰剂相比,阿巴洛肽使新椎体骨折的发生率降低了 86%。此外,与安慰剂和特立帕肽相比,阿巴洛肽在所有测量部位都实现了更大的 BMD 增加。基于这些结果,阿巴洛肽于 2017 年 4 月获得了 FDA 的批准。这篇综述讨论了这两种药物在疗效和安全性方面的现有数据,以及它们未来的可能应用。