Department of Hematology and Hematopoietic Cell Transplantation, City of Hope National Medical Center, Duarte, CA.
Alliance Statistics and Data Center, Mayo Clinic, Rochester, MN.
Blood Adv. 2023 Jan 24;7(2):196-204. doi: 10.1182/bloodadvances.2022007791.
Asparaginase is a key component of pediatric-inspired regimens in young adults with acute lymphoblastic leukemia (ALL). Truncation of asparaginase therapy is linked to inferior outcomes in children with ALL. However, a similar correlation in adults is lacking. Here, we studied the prevalence and risk factors associated with pegylated (PEG)-asparaginase discontinuation in young adults with ALL treated on the US intergroup Cancer and Leukemia Group B (CALGB) 10403 study and examined the prognostic impact of early discontinuation (ED) (defined as <4 of 5 or 6 planned doses) on survival outcomes. The analysis included 176 patients who achieved complete remission and initiated the delayed intensification (DI) cycle. The median number of PEG-asparaginase doses administered before DI was 5 (range, 1-6), with 57 (32%) patients with ED. The ED patients were older (median, 26 vs 23 years; P = .023). Survival was apparently lower for ED patients compared with those receiving ≥4 doses, but this finding was not statistically significant (hazard ratio [HR], 1.82; 95% confidence interval [CI], 0.97-3.43; P = .06), with corresponding 5-year overall survival (OS) rates of 66% and 80%, respectively. In patients with standard-risk ALL, the ED of PEG-asparaginase adversely influenced OS (HR, 2.3; 95% CI, 1.02-5.22; P = .04) with a trend toward inferior event-free survival (EFS) (HR, 1.84; 95% CI, 0.92-3.67; P = .08). In contrast, there was no impact of early PEG-asparaginase discontinuation on OS (P = .64) or EFS (P = .32) in patients with high-risk disease based on the presence of high-risk cytogenetics, Ph-like genotype, and/or high white blood cell count at presentation. In conclusion, early PEG-asparaginase discontinuation is common in young adults with ALL and may adversely impact survival of patients with standard-risk ALL.
门冬酰胺酶是儿童急性淋巴细胞白血病(ALL)方案中的关键组成部分。在 ALL 患儿中,门冬酰胺酶治疗的截断与较差的结果有关。然而,成人中缺乏类似的相关性。在这里,我们研究了在美国癌症和白血病组 B(CALGB)10403 研究中接受治疗的年轻 ALL 成人中聚乙二醇(PEG)-门冬酰胺酶停药的流行率和相关因素,并检查了早期停药(ED)(定义为<4 次)对生存结果的预后影响计划剂量中的 5 次或 6 次)。该分析包括 176 名达到完全缓解并开始延迟强化(DI)周期的患者。在开始 DI 之前,PEG-门冬酰胺酶的中位数剂量为 5(范围 1-6),57 名(32%)患者出现 ED。ED 患者年龄较大(中位数 26 岁比 23 岁;P=0.023)。与接受≥4 次剂量的患者相比,ED 患者的生存率显然较低,但这一发现无统计学意义(风险比 [HR],1.82;95%置信区间 [CI],0.97-3.43;P=0.06),相应的 5 年总生存率(OS)分别为 66%和 80%。在标准风险 ALL 患者中,PEG-门冬酰胺酶的 ED 对 OS 产生不利影响(HR,2.3;95%CI,1.02-5.22;P=0.04),EFS 呈下降趋势(HR,1.84;95%CI,0.92-3.67;P=0.08)。相比之下,在基于高风险细胞遗传学、Ph 样基因型和/或高白细胞计数的高危疾病患者中,早期 PEG-门冬酰胺酶停药对 OS(P=0.64)或 EFS(P=0.32)无影响。总之,年轻 ALL 成人中早期 PEG-门冬酰胺酶停药很常见,可能对标准风险 ALL 患者的生存产生不利影响。