Kim Inhye, Medina Scott H
Department of Biomedical Engineering, Pennsylvania State University, University Park, PA, 16802-4400, USA.
Department of Biomedical Engineering, Pennsylvania State University, University Park, PA, 16802-4400, USA; Huck Institutes of the Life Sciences, Pennsylvania State University, University Park, PA, 16802-4400, USA.
Biomaterials. 2025 Jul;318:123146. doi: 10.1016/j.biomaterials.2025.123146. Epub 2025 Jan 25.
Amyloid β (Aβ) assemblies exist not only in the central nervous system, but can circulate within the bloodstream to trigger and exacerbate peripheral, cerebrovascular, and neurodegenerative disorders. Eliminating excess peripheral Aβ fibrils, therefore, holds promise to improve the management of amyloid-related diseases. Here, we present nanoemulsion-mediated ultrasonic ablation of circulating Aβ fibrils to both destroy established plaques and prevent the re-growth of ablated fragments back into toxic species. This approach is made possible using a de novo designed peptide emulsifier that contains the self-associating sequence from the amyloid precursor protein. Emulsification of the peptide surfactant with fluorous nanodroplets produces contrast agents that rapidly adsorb Aβ assemblies and allows their ultrasound-controlled destruction via acoustic cavitation. Vessel-mimetic flow experiments demonstrate that nanoemulsion-assisted Aβ disruption can be achieved in circulation using clinical diagnostic ultrasound transducers. Additional cell-based assays confirm the ablated fragments are less toxic to neuronal and glial cells compared to mature fibrils, and can be rapidly phagocytosed by both peripheral and brain macrophages. These results highlight the potential of nanoemulsion contrast agents to deliver new imaging enabled strategies for non-invasive management of Aβ-related diseases using traditional diagnostic ultrasound modalities.
淀粉样β蛋白(Aβ)聚集体不仅存在于中枢神经系统中,还能在血液循环中循环,引发并加剧外周、脑血管和神经退行性疾病。因此,消除多余的外周Aβ纤维有望改善淀粉样相关疾病的治疗。在此,我们展示了纳米乳液介导的循环Aβ纤维超声消融,既能破坏已形成的斑块,又能防止消融后的碎片重新生长为有毒物质。这种方法通过一种从头设计的肽乳化剂得以实现,该乳化剂包含淀粉样前体蛋白的自缔合序列。肽表面活性剂与含氟纳米液滴乳化产生造影剂,可快速吸附Aβ聚集体,并通过声空化作用实现超声控制下的破坏。血管模拟流动实验表明,使用临床诊断超声换能器可在循环中实现纳米乳液辅助的Aβ破坏。其他基于细胞的试验证实,与成熟纤维相比,消融后的碎片对神经元和神经胶质细胞的毒性较小,并且能被外周和脑巨噬细胞快速吞噬。这些结果突出了纳米乳液造影剂利用传统诊断超声模式为Aβ相关疾病的非侵入性治疗提供新的成像支持策略的潜力。