Fernández-Soto Paulina, Casulli Joshua, Solano-Castro Danilo, Rodríguez-Fernández Pablo, Jowitt Thomas A, Travis Mark A, Cavet Jennifer S, Tabernero Lydia
School of Biological Sciences, Faculty of Biology Medicine and Health, Manchester Academic Health Science Centre, University of Manchester, Manchester, M13 9PT, UK.
Lydia Becker Institute for Immunology and Inflammation, University of Manchester, Manchester, UK.
Sci Rep. 2021 Apr 7;11(1):7667. doi: 10.1038/s41598-021-87117-x.
SapM is a secreted virulence factor from Mycobacterium tuberculosis critical for pathogen survival and persistence inside the host. Its full potential as a target for tuberculosis treatment has not yet been exploited because of the lack of potent inhibitors available. By screening over 1500 small molecules, we have identified new potent and selective inhibitors of SapM with an uncompetitive mechanism of inhibition. The best inhibitors share a trihydroxy-benzene moiety essential for activity. Importantly, the inhibitors significantly reduce mycobacterial burden in infected human macrophages at 1 µM, and they are selective with respect to other mycobacterial and human phosphatases. The best inhibitor also reduces intracellular burden of Francisella tularensis, which secretes the virulence factor AcpA, a homologue of SapM, with the same mechanism of catalysis and inhibition. Our findings demonstrate that inhibition of SapM with small molecule inhibitors is efficient in reducing intracellular mycobacterial survival in host macrophages and confirm SapM as a potential therapeutic target. These initial compounds have favourable physico-chemical properties and provide a basis for exploration towards the development of new tuberculosis treatments. The efficacy of a SapM inhibitor in reducing Francisella tularensis intracellular burden suggests the potential for developing broad-spectrum antivirulence agents to treat microbial infections.
SapM是结核分枝杆菌分泌的一种毒力因子,对病原体在宿主体内的存活和持续存在至关重要。由于缺乏有效的抑制剂,其作为结核病治疗靶点的全部潜力尚未得到开发。通过筛选1500多种小分子,我们发现了新型强效且具有选择性的SapM抑制剂,其抑制机制为非竞争性。最佳抑制剂具有一个对活性至关重要的三羟基苯部分。重要的是,这些抑制剂在1µM时能显著降低感染人巨噬细胞中的分枝杆菌负荷,并且对其他分枝杆菌和人磷酸酶具有选择性。最佳抑制剂还能降低土拉弗朗西斯菌的细胞内负荷,该菌分泌毒力因子AcpA,它是SapM的同源物,具有相同的催化和抑制机制。我们的研究结果表明,用小分子抑制剂抑制SapM可有效降低宿主巨噬细胞内分枝杆菌的存活率,并证实SapM是一个潜在的治疗靶点。这些初始化合物具有良好的物理化学性质,为探索开发新的结核病治疗方法提供了基础。SapM抑制剂降低土拉弗朗西斯菌细胞内负荷的功效表明,开发广谱抗毒力药物治疗微生物感染具有潜力。